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Project Cure SMA is a collaborative initiative between Families of SMA and clinical investigators designed to help facilitate the rapid translation of promising new therapies to individuals with SMA. The primary goal of Project Cure SMA is to develop safe and well-tolerated clinical protocols to help identify effective therapies for SMA.

• Spinal Muscular Atrophy: Classification, Diagnosis, Management, Pathogenesis, and Future Research Directions by Felina V. Kostova, Virginia C. Williams, Jill Heemskerk, Susan Iannaccone, Christine DiDonato, Kathryn J. Swoboda, and Bernard L. Maria - published in Journal of Child Neurology 2007; 22: 926-45.

• Perspectives on clinical trials in spinal muscular atrophy by Kathryn J. Swoboda, John T. Kissel, Thomas O. Crawford, Mark B. Bromberg, Gyula Acsadi, Guy D'Anjou, Kristin J. Krosschell, Sandra P. Reyna, Mary K. Schroth, Charles B. Scott, and Louise R. Simard -  published in Journal of Child Neurology 2007; 22: 957-66.

• Congenital Bone Fractures in Spinal Muscular Atrophy: Functional Role for SMN Protein in Bone Remodeling by Srinivasan Shanmugarajan, Kathryn J. Swoboda, Susan T. Iannaccone, William L. Ries, Bernard L. Maria, Sakamuri V. Reddy - published in Journal of Child Neurology 2007; 22: 967-973

• Spinal Muscular Atrophy Genetic Counseling Access and Genetic Knowledge: Parents' Perspectives by Candice Meldrum, Charles Scott, and Kathryn J. Swoboda - published in Journal of Child Neurology 2007; 22:1019-26.

• Preclinical Validation of a Multiplex Real-time Assay to Quantify SMN mRNA in Patients with SMA by Louise R. Simard, MC Bélanger, S. Morissette, Mark Wride,Thomas W. Prior, and Kathryn J. Swoboda - published in Neurology 2007; 68: 451-6. http://www.neurology.org/cgi/content/full/68/6/451

• A modified Hamersmith functional motor scale for use in multi-center research on SMA by Kristin J. Krosschell, Jo Anne Maczulski, Thomas O. Crawford, Charles Scott,  and Kathryn J. Swoboda - published in Neuromuscular Disorders xx (2006) 1–10